Lentiviral vectors containing a retinal pigment epithelium specific promoter for leber congenital amaurosis gene therapy. Lentiviral gene therapy for LCA

Details

Serval ID
serval:BIB_020E63756414
Type
Article: article from journal or magazin.
Collection
Publications
Institution
Title
Lentiviral vectors containing a retinal pigment epithelium specific promoter for leber congenital amaurosis gene therapy. Lentiviral gene therapy for LCA
Journal
Advances in Experimental Medicine and Biology
Author(s)
Bemelmans  A. P., Kostic  C., Hornfeld  D., Jaquet  M., Crippa  S. V., Hauswirth  W. W., Lem  J., Wang  Z., Schorderet  D. E., Munier  F. L., Wenzel  A., Arsenijevic  Y.
ISSN
0065-2598 (Print)
Publication state
Published
Issued date
2006
Volume
572
Pages
247-53
Notes
Journal Article
Research Support, Non-U.S. Gov't
Keywords
Animals Carrier Proteins/genetics Electroretinography/methods Eye Proteins/genetics Gene Therapy/*methods *Genetic Vectors Green Fluorescent Proteins/metabolism Humans Lentivirus/*genetics/metabolism Mice Mice, Knockout Optic Atrophy, Hereditary, Leber/*genetics/*therapy Pigment Epithelium of Eye/*metabolism *Promoter Regions (Genetics) Retina/metabolism
Pubmed
Web of science
Create date
28/01/2008 13:58
Last modification date
20/08/2019 13:24
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