Lentiviral vectors containing a retinal pigment epithelium specific promoter for leber congenital amaurosis gene therapy. Lentiviral gene therapy for LCA

Détails

ID Serval
serval:BIB_020E63756414
Type
Article: article d'un périodique ou d'un magazine.
Collection
Publications
Institution
Titre
Lentiviral vectors containing a retinal pigment epithelium specific promoter for leber congenital amaurosis gene therapy. Lentiviral gene therapy for LCA
Périodique
Advances in Experimental Medicine and Biology
Auteur⸱e⸱s
Bemelmans  A. P., Kostic  C., Hornfeld  D., Jaquet  M., Crippa  S. V., Hauswirth  W. W., Lem  J., Wang  Z., Schorderet  D. E., Munier  F. L., Wenzel  A., Arsenijevic  Y.
ISSN
0065-2598 (Print)
Statut éditorial
Publié
Date de publication
2006
Volume
572
Pages
247-53
Notes
Journal Article
Research Support, Non-U.S. Gov't
Mots-clé
Animals Carrier Proteins/genetics Electroretinography/methods Eye Proteins/genetics Gene Therapy/*methods *Genetic Vectors Green Fluorescent Proteins/metabolism Humans Lentivirus/*genetics/metabolism Mice Mice, Knockout Optic Atrophy, Hereditary, Leber/*genetics/*therapy Pigment Epithelium of Eye/*metabolism *Promoter Regions (Genetics) Retina/metabolism
Pubmed
Web of science
Création de la notice
28/01/2008 13:58
Dernière modification de la notice
20/08/2019 13:24
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