Mutations in MMP9 and MMP13 determine the mode of inheritance and the clinical spectrum of metaphyseal anadysplasia.

Details

Serval ID
serval:BIB_F68A9DE136FD
Type
Article: article from journal or magazin.
Collection
Publications
Title
Mutations in MMP9 and MMP13 determine the mode of inheritance and the clinical spectrum of metaphyseal anadysplasia.
Journal
American Journal of Human Genetics
Author(s)
Lausch E., Keppler R., Hilbert K., Cormier-Daire V., Nikkel S., Nishimura G., Unger S., Spranger J., Superti-Furga A., Zabel B.
ISSN
1537-6605 (Electronic)
ISSN-L
0002-9297
Publication state
Published
Issued date
2009
Volume
85
Number
2
Pages
168-178
Language
english
Abstract
The matrix metalloproteinases MMP9 and MMP13 catalyze the degradation of extracellular matrix (ECM) components in the growth plate and at the same time cleave and release biologically active molecules stored in the ECM, such as VEGFA. In mice, ablation of Mmp9, Mmp13, or both Mmp9 and Mmp13 causes severe distortion of the metaphyseal growth plate. We report that mutations in either MMP9 or MMP13 are responsible for the human disease metaphyseal anadysplasia (MAD), a heterogeneous group of disorders for which a milder recessive variant and a more severe dominant variant are known. We found that recessive MAD is caused by homozygous loss of function of either MMP9 or MMP13, whereas dominant MAD is associated with missense mutations in the prodomain of MMP13 that determine autoactivation of MMP13 and intracellular degradation of both MMP13 and MMP9, resulting in a double enzymatic deficiency.
Keywords
Adolescent, Adult, Amino Acid Sequence, Animals, Asian Continental Ancestry Group/genetics, Asian Continental Ancestry Group/statistics & numerical data, Base Sequence, Case-Control Studies, Child, Child, Preschool, Collagenases/metabolism, Female, Gene Frequency, Heterozygote, Homozygote, Humans, Infant, Matrix Metalloproteinase 13/genetics, Matrix Metalloproteinase 13/metabolism, Matrix Metalloproteinase 9/blood, Matrix Metalloproteinase 9/genetics, Mice, Mice, Knockout, Models, Molecular, Molecular Sequence Data, Mutation, NIH 3T3 Cells, Osteochondrodysplasias/genetics, Osteochondrodysplasias/radiography, Pedigree, Skin/cytology, Young Adult
Pubmed
Web of science
Open Access
Yes
Create date
14/03/2011 17:09
Last modification date
20/08/2019 17:23
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