A novel form of complete IL-12/IL-23 receptor beta1 deficiency with cell surface-expressed nonfunctional receptors

Details

Serval ID
serval:BIB_78BD5FBBC6CC
Type
Article: article from journal or magazin.
Collection
Publications
Title
A novel form of complete IL-12/IL-23 receptor beta1 deficiency with cell surface-expressed nonfunctional receptors
Journal
Blood
Author(s)
Fieschi C., Bosticardo M., de Beaucoudrey L., Boisson-Dupuis S., Feinberg J., Santos O. F., Bustamante J., Levy J., Candotti F., Casanova J. L.
ISSN
0006-4971 (Print)
ISSN-L
0006-4971
Publication state
Published
Issued date
2004
Volume
104
Number
7
Pages
2095-101
Language
english
Notes
Fieschi, Claire
Bosticardo, Marita
de Beaucoudrey, Ludovic
Boisson-Dupuis, Stephanie
Feinberg, Jacqueline
Santos, Orchidee Filipe
Bustamante, Jacinta
Levy, Jacov
Candotti, Fabio
Casanova, Jean-Laurent
eng
Case Reports
Research Support, Non-U.S. Gov't
Blood. 2004 Oct 1;104(7):2095-101. Epub 2004 Jun 3.
Abstract
Complete interleukin-12/interleukin-23 receptor beta1 (IL-12Rbeta1) deficiency is the most frequent known genetic etiology of the syndrome of Mendelian susceptibility to mycobacterial disease. The patients described to date lack IL-12Rbeta1 at the surface of their natural killer (NK) and T cells due to IL12RB1 mutations, which either interrupt the open reading frame or disrupt protein folding. We describe a patient with a large in-frame deletion of 12165 nucleotides (nt) in IL12RB1, encompassing exons 8 to 13 and resulting in the surface expression of nonfunctional IL-12Rbeta1. These 6 exons encode the proximal NH2-terminal half of the extracellular domain downstream from the cytokine-binding domain. Five of 6 monoclonal anti-IL-12Rbeta1 antibodies tested recognized the internally truncated chain on the cell surface. However, IL-12 and IL-23 did not bind normally to the patient's IL-12Rbeta1-containing respective heterodimeric receptors. As a result, signal transducer and activator of transcription-4 (STAT4) was not phosphorylated and interferon-gamma (IFN-gamma) production was not induced in the patient's cells upon stimulation with even high doses of IL-12 or IL-23. The functional defect was completely rescued by retrovirus-mediated IL-12Rbeta1 gene transfer. Thus, the detection of IL-12Rbeta1 on the cell surface does not exclude the possibility of complete IL-12Rbeta1 deficiency in patients with mycobacteriosis or salmonellosis. Paradoxically, the largest IL12RB1 mutation detected is associated with the cell surface expression of nonfunctional IL-12Rbeta1, defining a novel genetic form of IL-12Rbeta1 deficiency.
Keywords
Antibodies, Monoclonal/chemistry, Cell Membrane/*metabolism, Cells, Cultured, Child, Cytokines/metabolism, DNA, Complementary/metabolism, DNA-Binding Proteins/metabolism, Enzyme-Linked Immunosorbent Assay, Exons, Flow Cytometry, Gene Deletion, Gene Transfer Techniques, Humans, Interferon-gamma/metabolism, Interleukin-12/metabolism, Interleukin-23, Interleukin-23 Subunit p19, Interleukins/*metabolism, Killer Cells, Natural/metabolism, Male, Models, Genetic, Mutation, Open Reading Frames, Phenotype, Phosphorylation, Polymerase Chain Reaction, Protein Folding, Protein Structure, Tertiary, RNA/metabolism, Receptors, Interleukin/deficiency/*metabolism, Receptors, Interleukin-12, Retroviridae/genetics, STAT4 Transcription Factor, Time Factors, Trans-Activators/metabolism
Pubmed
Create date
01/11/2017 11:29
Last modification date
20/08/2019 15:35
Usage data