Hematopoietic Stem- and Progenitor-Cell Gene Therapy for Hurler Syndrome

Details

Serval ID
serval:BIB_4BB789839CEB
Type
Article: article from journal or magazin.
Collection
Publications
Title
Hematopoietic Stem- and Progenitor-Cell Gene Therapy for Hurler Syndrome
Journal
New England Journal of Medicine
Author(s)
Gentner Bernhard, Tucci Francesca, Galimberti Stefania, Fumagalli Francesca, De Pellegrin Maurizio, Silvani Paolo, Camesasca Chiara, Pontesilli Silvia, Darin Silvia, Ciotti Francesca, Sarzana Marina, Consiglieri Giulia, Filisetti Chiara, Forni Giulia, Passerini Laura, Tomasoni Daniela, Cesana Daniela, Calabria Andrea, Spinozzi Giulio, Cicalese Maria-Pia, Calbi Valeria, Migliavacca Maddalena, Barzaghi Federica, Ferrua Francesca, Gallo Vera, Miglietta Simona, Zonari Erika, Cheruku Patali S., Forni Claudia, Facchini Marcella, Corti Ambra, Gabaldo Michela, Zancan Stefano, Gasperini Serena, Rovelli Attilio, Boelens Jaap-Jan, Jones Simon A., Wynn Robert, Baldoli Cristina, Montini Eugenio, Gregori Silvia, Ciceri Fabio, Valsecchi Maria G., la Marca Giancarlo, Parini Rossella, Naldini Luigi, Aiuti Alessandro, Bernardo Maria-Ester
ISSN
0028-4793
1533-4406
Publication state
Published
Issued date
18/11/2021
Volume
385
Number
21
Pages
1929-1940
Language
english
Keywords
General Medicine
Pubmed
Web of science
Create date
13/07/2022 16:38
Last modification date
14/07/2022 6:37
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