Mutations of Jak-3 gene in patients with autosomal severe combined immune deficiency (SCID)

Details

Serval ID
serval:BIB_BBE5389EC071
Type
Article: article from journal or magazin.
Collection
Publications
Title
Mutations of Jak-3 gene in patients with autosomal severe combined immune deficiency (SCID)
Journal
Nature
Author(s)
Macchi P., Villa A., Giliani S., Sacco M. G., Frattini A., Porta F., Ugazio A. G., Johnston J. A., Candotti F., O'Shea J. J.
Working group(s)
et al.
ISSN
0028-0836 (Print)
ISSN-L
0028-0836
Publication state
Published
Issued date
1995
Volume
377
Number
6544
Pages
65-8
Language
english
Notes
Macchi, P
Villa, A
Giliani, S
Sacco, M G
Frattini, A
Porta, F
Ugazio, A G
Johnston, J A
Candotti, F
O'Shea, J J
eng
Research Support, Non-U.S. Gov't
England
Nature. 1995 Sep 7;377(6544):65-8.
Abstract
Severe combined immune deficiency (SCID) represents a heterogenous group of hereditary diseases. Mutations in the common gamma-chain (gamma c), which is part of several cytokine receptors including those for interleukin (IL)-2, IL-4, IL-7, IL-9 and IL-15, are responsible for X-linked SCID, which is usually associated with a lack of circulating T cells and the presence of B lymphocytes (T- B+ SCID). The gene(s) responsible for autosomal recessive T- B+ SCID is still unknown. The Jak-3 protein kinase has been found to associate with the gamma c-chain-containing cytokine receptors. Therefore Jak-3 or other STAT proteins with which it interacts are candidate genes for autosomal recessive T- B+ SCID. Here we investigate two unrelated T- B+ SCID patients (both from consanguineous parents) who have homozygous mutations in the gene for Jak-3. One patient carries a mutation (Tyr100-->Cys) in a conserved tyrosine residue in the JH7 domain of Jak-3 which is absent in more than 150 investigated chromosomes. The other patient carries a homozygous 151-base-pair deletion in the kinase-like domain, leading to a frameshift and premature termination. Both mutations resulted in markedly reduced levels of Jak-3. These findings show that abnormalities in the Jak/STAT signalling pathway can account for SCID in humans.
Keywords
B-Lymphocytes/immunology, Base Sequence, Cell Line, Transformed, DNA Mutational Analysis, DNA Primers, Humans, Janus Kinase 3, Molecular Sequence Data, *Mutation, Polymerase Chain Reaction, Protein-Tyrosine Kinases/deficiency/*genetics, Sequence Deletion, Severe Combined Immunodeficiency/enzymology/*genetics/immunology, T-Lymphocytes/immunology
Pubmed
Create date
01/11/2017 11:29
Last modification date
20/08/2019 16:29
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