Positron emission tomography imaging demonstrates correlation between behavioral recovery and correction of dopamine neurotransmission after gene therapy.

Details

Serval ID
serval:BIB_046AA371D042
Type
Article: article from journal or magazin.
Collection
Publications
Title
Positron emission tomography imaging demonstrates correlation between behavioral recovery and correction of dopamine neurotransmission after gene therapy.
Journal
Journal of Neuroscience
Author(s)
Leriche L., Björklund T., Breysse N., Besret L., Grégoire M.C., Carlsson T., Dollé F., Mandel R.J., Déglon N., Hantraye P., Kirik D.
ISSN
1529-2401 (Electronic)
ISSN-L
0270-6474
Publication state
Published
Issued date
2009
Volume
29
Number
5
Pages
1544-1553
Language
english
Notes
Publication types: Comparative Study ; Journal Article ; Research Support, Non-U.S. Gov'tPublication Status: ppublish
Abstract
In vivo gene transfer using viral vectors is an emerging therapy for neurodegenerative diseases with a clinical impact recently demonstrated in Parkinson's disease patients. Recombinant adeno-associated viral (rAAV) vectors, in particular, provide an excellent tool for long-term expression of therapeutic genes in the brain. Here we used the [(11)C]raclopride [(S)-(-)-3,5-dichloro-N-((1-ethyl-2-pyrrolidinyl)methyl)-2-hydroxy-6-methoxybenzamide] micro-positron emission tomography (PET) technique to demonstrate that delivery of the tyrosine hydroxylase (TH) and GTP cyclohydrolase 1 (GCH1) enzymes using an rAAV5 vector normalizes the increased [(11)C]raclopride binding in hemiparkinsonian rats. Importantly, we show in vivo by microPET imaging and postmortem by classical binding assays performed in the very same animals that the changes in [(11)C]raclopride after viral vector-based enzyme replacement therapy is attributable to a decrease in the affinity of the tracer binding to the D(2) receptors, providing evidence for reconstitution of a functional pool of endogenous dopamine in the striatum. Moreover, the extent of the normalization in this non-invasive imaging measure was highly correlated with the functional recovery in motor behavior. The PET imaging protocol used in this study is fully adaptable to humans and thus can serve as an in vivo imaging technique to follow TH + GCH1 gene therapy in PD patients and provide an additional objective measure to a potential clinical trial using rAAV vectors to deliver l-3,4-dihydroxyphenylanaline in the brain.
Keywords
Animals, Behavior, Animal/physiology, Corpus Striatum/metabolism, Dependovirus/genetics, Dopamine/biosynthesis, Dopamine/genetics, Gene Therapy/methods, Genetic Vectors/administration & dosage, Genetic Vectors/biosynthesis, Humans, Male, Parkinsonian Disorders/genetics, Parkinsonian Disorders/metabolism, Positron-Emission Tomography/methods, Rats, Rats, Sprague-Dawley, Synaptic Transmission/genetics, Transgenes
Pubmed
Web of science
Open Access
Yes
Create date
13/12/2011 17:15
Last modification date
20/08/2019 13:26
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